Junk DNA in Birds Inspires New Technique in Inserting Codes Into Genomes, Unlocks Safe and Efficient Gene Therapy

Medicine & Technology Feb 23, 2024

A new technique uses retrotransposon from birds to insert genes into the genome, paving the way for improved gene therapy. Find out more about it in this article.

Butterfly Children With Fragile Skin May Be Treated Using Novel Gene Therapy in Topical Form

Jun 13, 2023

The Food and Drug Administration has granted approval on the use of Vyjuvek as the first topical gene therapy against dystrophic epidermolysis bullosa. Continue reading to find out more.

$3.6M Gene Therapy For Metachromatic Leukodystrophy Saves Toddler But Not Her Sister [Report]

Feb 15, 2023

A multi-million gene therapy saved a toddler diagnosed with metachromatic leukodystrophy. Continue reading for full details.

Gene Therapy Prevents Blindness in Children With Leber Congenital Amaurosis, NPHP5 Deficiency Expained

Sep 08, 2022

Scientists developed a gene therapy that can help in the prevention of blindness in children. Continue reading to know more about gene rehabilitation.

Tay-Sachs Disease Treatment: Two Children Became First-Ever Successful Gene Therapy, After 14 Years of Development

Feb 16, 2022

Two babies have recently been reported to have been given the first-ever treatment for a severe neurological disease called Tay-Sachs disease after more than 14 years of development.

Polypeptide Nanoparticle Designed to Adapt to Gene Therapy Cargo For a More Efficient Delivery System

Jun 11, 2021

Researchers have developed a new nanoparticle vector made from polypeptide-based materials that are adaptable to various therapies, including gene therapy, for a more effective delivery system.

Potential Gene Therapy for Alzheimer's Disease Prevents Memory Loss, Strengthens Learning Abilities

May 05, 2021

Researchers at the University of California - San Diego have successfully tested using mouse models a potential gene therapy for Alzheimer's Disease that preserves memory and learning abilities.

Gene Therapy Offers Cure for Blindness since Infancy, Study Shows

Apr 03, 2021

Study findings revealed that gene therapy provided vision to patients suffering from a rare form of genetic form blindness since childhood.

New Gene Therapy Method Includes Microneedles and Nanoparticles

Oct 07, 2020

A new method of gene therapy involves minimally invasive microneedles. The patch includes genetic material within nanoparticles and can be applied for various clinical uses such as cancers, diseases, and vaccines.

New CRISPR Technology Could Potentially Cure More Diseases Efficiently

Oct 22, 2019

A new CRISPR-based technology for genome editing called prime editing is more efficient and reliable compared to old techniques, potentially curing 89% of all known genetic conditions.

'Bubble Boy' Babies Freed From Life of Isolation by Experimental Gene Therapy

Apr 22, 2019

Treatment restores immune-system function in young children with severe disorder.

Pfizer Explores Gene Therapy In Developing Treatment For Rare Diseases

Dec 09, 2014

Despite the number of mixed results in gene therapy which has had its share of setbacks, drug company giant Pfizer Inc. is pushing through with its gene therapy project. This is backed by advancement in technology and better research facilities, and for its first project, a partnership with privately-owned biotech firm Spark Therapeutics.